Sickle cell disease is a devastating, inherited blood disorder that affects an estimated eight million people worldwide and roughly 100,000 here in the United States, most of them African American. It ...

Ernexa is advancing a best-in-class approach using synthetic, allogeneic iMSCs to provide a scalable, off-the-shelf treatment without needing patient-specific cell harvesting. The Company continues to ...

Chinese scientists have identified a key mechanism that governs the function of plant stem cells — cells that enable plants to continuously generate new leaves, stems and flowers — a finding that ...

Almost two thirds of patients with T-cell acute lymphoblastic leukaemia involved in a clinical trial of the treatment are now ...

To meet ambitious U.S. Department of Energy targets for sustainable aviation fuel (SAF), production of purpose-grown energy ...

In a Maryland operating room one day in November 2025, doctors made medical history by transplanting a genetically modified ...

Scientists have developed a new method to boost the energy of aging or damaged cells, an innovation that could improve ...

Akhilesh Gaharwar and PhD student John Soukar, along with their fellow researchers from the Department of Biomedical ...

The publication, titled “Prime Editing for p47-phox Chronic Granulomatous Disease,” reports initial data for two patients treated in the Phase 1/2 trial of PM359, which was designed to assess safety, ...

The first study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia ...

The chief medical officer of Genetix Biotherapeutics, formerly known as Bluebird bio, discusses timelines and operational ...

The patient died from vent-occlusive liver disease, a well-characterized side effect of the busulfan, the myeloablative chemotherapy used to prepare the bone marrow for engraftment with the ...